Tailored antisense oligonucleotides for ultrarare CNS diseases: An experience-based best practice framework for individual patient evaluation
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Author:
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Schule, Rebecca; Graessner, Holm; Aartsma-Rus, Annemieke; van Roon-Mom, Willeke M. C.; Synofzik, Matthis
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Tübinger Autor(en):
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Published in:
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Molecular Therapy Nucleic Acids
(2025), Bd.
36 (3),
Article 102615
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Verlagsangabe:
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Cambridge : Cell Press
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Language:
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English
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Full text:
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http://dx.doi.org/10.1016/j.omtn.2025.102615
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ISSN:
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2162-2531
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DDC Classifikation:
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610 - Medicine and health
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Dokumentart:
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Article
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